Tag: lysosomal
Experts laud Karnataka govt’s timely initiatives for rare diseases patients
Karnataka government has been providing treatment to adult-onset Pompe patients and Gaucher patients since 2016. Experts feel other governments must learn from this example..................
Rare disease day commemorated in Delhi
Lysosomal Storage Disorders Support Society (LSDSS) organized an event to spread awareness regarding rare diseases and its policy...................
Indian startup develops drug for key orphan diseases, partners US firm
Oraxion Therapeutics, a spin-off from Aten Porus Lifesciences has entered into an agreement with a US-based biopharma company to license its lead asset ORX-301 for the treatment of Niemann-Pick Type C disorder and Focal Segmental Glomerulosclerosis.......................