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SynaptixBio expands collaboration with Evotec to advance treatments for H-ABC

The extended partnership aims to develop new therapies for severe TUBB4A leukodystrophy, building on research from CHOP

SynaptixBio awarded second FDA Orphan Drug Designation to boost search for...

The leading biotech company is now aiming to develop treatment for second variant of TUBB4A leukodystrophy