Tag: TUBB4a leukodystrophy
SynaptixBio awarded second FDA Orphan Drug Designation to boost search for...
The leading biotech company is now aiming to develop treatment for second variant of TUBB4A leukodystrophy
Thousands of patients could have rare life-threatening diseases without knowing it,...
TUBB4a leukodystrophy - an incurable genetic condition that damages the central nervous system and can be deadly to babies and young children