Tag: Orphan Drug
SynaptixBio awarded second FDA Orphan Drug Designation to boost search for...
The leading biotech company is now aiming to develop treatment for second variant of TUBB4A leukodystrophy
Lupin signs distribution agreement with Medis for orphan drug, NaMuscla
Agreement enables expanded patient access of the only EU-approved treatment for myotonia symptoms in non-dystrophic myotonic disorders in Central and Eastern European territories
Zydus Cadila’s Saroglitazar granted ‘Orphan Drug Designation’ by USFDA
Saroglitazar Mg is a potent and selective peroxisome proliferator-activated receptor alpha and gamma dual agonist used in the treatment of patients with Primary Biliary Cholangitis (PBC)........................